The Gene Therapy Toolbox: AAV
Date/Time: Wednesday, October 7, 2020 - 12:30 PM – 1:45 PM
Track: Interactive Workshop
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Description:
Following the approval of the first gene therapy for a neurological disease, a growing number of clinical trials predicts additional approvals in the next decade, most using AAV as a vehicle. Neurologists should familiarize with the status of the field for these “one and done” therapies.
Objective(s):
To understand the biology of AAV, repertoire of capsids, species specificity and immune responses.
To learn the different AAV-driven therapeutic strategies available.
To identify currently approved and emerging AAV-based therapies for neurological diseases.